Oligonucleotidesagainst a splicingenhancer sequence ledto dystrophinproduction in musclecells from a Duchennemuscular dystrophypatient Yasuhiro TakeshimaHiroko WadaMariko Yagi2001 год

Oligonucleotides against a splicing enhancer sequence led to dystrophin production in muscle cells from a Duchenne muscular dystrophy patient
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